BioMarin Collaborates with Allen Institute to Develop Gene Therapies for Rare Brain Diseases

 BioMarin Collaborates with Allen Institute to Develop Gene Therapies for Rare Brain Diseases

BioMarin Collaborates with Allen Institute to Develop Gene Therapies for Rare Brain Diseases

Shots:

  • BioMarin will receive an exclusive license to each program for research, development, and commercialization of the gene therapies
  • The collaboration will utilize Allen institute technologies to develop new gene therapies for rare genetic diseases of CNS by targeting gene expression to specific cells
  • Allen Institute has developed modified engineering AAVs to carry genes on specific types of neurons or other cells in the brain

Click here to­ read full press release/ article | Ref: BioMarin | Image: BioMarin