Shots: • Galafold is a first precision and oral drug (Q2D) for 348 amenable galactosidase alpha gene (GLA) variants to treat Fabry in U.S. • The approval was under Subpart […]readmore
Tags : 15 Yrs.
Shots: Alnylam’s siRNA molecule Onpattro receives FDA approval for fatal genetic disorder polyneuropathy caused by hereditary transthyretin-mediated amyloidosis (hATTR) Approval is based on results from Ph III APOLLO study involving […]readmore